Conditions We Treat

The Blood & Marrow Transplant Program at the Center for Cancer and Blood Disorders treats a wide range of conditions and diseases, including:

• Leukemia: Cancer that starts in immature blood cells; the most common form of childhood blood cancers
• Lymphoma: A type of cancer that develops when white blood cells grow uncontrollably
• Myelodysplastic syndromes: A group of disorders in which blood cells in the bone marrow do not mature properly
• Histiocytic disorders: A rare blood disease that causes abnormal cell growth that is not necessarily cancer

• Brain cancers: An abnormal growth of tissue in the brain
• Ewing sarcoma: An aggressive form of cancer that forms in bone or soft tissue 
• Germ cell tumor: A tumor that develops from cells that were designed to become sperm or eggs
• Neuroblastoma: Tumors that form when immature nerve cells in the nervous system grow out of control
• Osteosarcoma: Tumors that begin in bone, usually the long bone at the end of the thigh
• Retinoblastoma: A curable kind of eye cancer that develops in the retina
• Rhabdomyosarcoma: A rare type of cancer that begins as a growth of cells that should be skeletal muscle
• Wilms tumor: The most common type of kidney cancer in children

• Aplastic anemia: A serious disease that prevents the blood from making enough new blood cells
• Sickle cell disease: A disorder that causes red blood cells to become sticky and shaped in the form of a crescent, or sickle
• Thrombocytopenia: A condition that causes a newborn baby to have too few platelets in their blood

• Chronic Granulomatous disease (CGD): An immune disorder that prevents white blood cells from effectively killing certain bacteria and fungi
• Leukocyte Adhesion Defect/Deficiency (LAD): An inherited immune system disorder that makes it difficult for the body to fight infections and heal wounds
• Primary Immune Regulatory Disorders (PIRDs): A rare disorder that keeps the body’s immune system from regulating itself
• Severe Combined Immunodeficiency (SCID): Causes a weakened immune system incapable of fighting off illness
• T Cell disorders: A group of conditions that affect how T cells function, weakening the immune system and making it harder for the body to fight infections
• Wiskott-Aldrich Syndrome (WAS): A rare condition that affects your child’s immune system and causes excessive bleeding

• Adrenoleukodystrophy (ALD): A genetic condition that damages the membrane that covers nerve cells in the brain and spinal cord
• Beta-glucuronidase deficiency (VII): A rare inherited disorder that causes developmental, skeletal and organ-related problems
• Gaucher disease: A rare inherited disorder that causes fatty substances to build up in organs and tissues
• Glycogen storage disease: A group of inherited disorders that affect how the body stores and uses sugar for energy
• Mucopolysaccharidoses (MPS): A group of rare inherited disorders that prevent the proper breakdown of certain sugars and cause them to build up, causing damage
• Hunter disease: A disorder that keeps the body from breaking down certain sugars, leading to a buildup that can affect growth, organs, bones and brain development over time
• Hurler syndrome (MPSI): A disorder in which the body cannot break down certain sugars, causing progressive damage to the bones, organs, heart and nervous system.
• I Cell disease: A rare inherited disorder that causes severe developmental delays, skeletal abnormalities and coarse facial features
• Leukodystrophies (Krabbe disease): Rare genetic disorders that damage the protective covering around nerve cells in the brain and nervous system
• Niemann-Pick disease: A group of genetic disorders that cause lipids to build up in body tissues
• Sanfilippo syndrome (III): A disorder that primarily affects the brain and spinal cord, often called childhood Alzheimer’s disease

• Graft Versus Host disease: A condition that causes immune cells from donated tissue to attack the recipient’s body